Choroideremia Natural History Study (4D-NHS.CHM-1): Open – enrollment completed
This natural history study aims to define retinal disease progression in CHM patients through serial ophthalmologic and OCT(Optical Coherence Tomography) evaluations in patients with a wide range of baseline disease severity. Approximately 45 patients were enrolled and followed according to the protocol. Patients will be followed for up to two years. A subset of these patients will be eligible for enrollment into the subsequent Phase 1-2 clinical trial of the 4DMT CHM product (see above).